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Clinical trial condition

Metabolism, Inborn Errors

Explore clinical trials studying Metabolism, Inborn Errors. Study availability and eligibility vary by location and protocol.

2,499 public trials 456 recruiting studies
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Metabolism, Inborn Errors trial results

Completed

Smith-Lemli-Opitz Syndrome and Cholic Acid

NCT03720990

Conditions
Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +9 more
Locations
  • Colorado Children's Hospital Aurora, Colorado, United States
  • University of Nebraska Medical Center Omaha, Nebraska, United States
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Completed

APOLLO: The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis

NCT01960348

Conditions
Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, +16 more
Locations
  • Clinical Trial Site La Mesa, California, United States
  • Clinical Trial Site Orange, California, United States
  • Clinical Trial Site Denver, Colorado, United States
  • Clinical Trial Site Chicago, Illinois, United States
View all 52 locations
View Trial Details
Completed

Patisiran in Patients With Hereditary Transthyretin-mediated Amyloidosis (hATTR Amyloidosis) Disease Progression Post-Liver Transplant

NCT03862807

Conditions
Amyloidosis, Amyloidosis, Familial, Amyloidosis, Hereditary, Transthyretin-Related, +7 more
Locations
  • Clinical Trial Site Créteil, France
  • Clinical Trial Site Le Kremlin-Bicêtre, France
  • Clinical Trial Site Münster, Germany
  • Clinical Trial Site Messina, Italy
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