Skip to main content
OpenTrials

Clinical trial condition

Metabolism, Inborn Errors

Explore clinical trials studying Metabolism, Inborn Errors. Study availability and eligibility vary by location and protocol.

13 public trials 2 recruiting studies
Refine in advanced search Browse all conditions

Metabolism, Inborn Errors trial results

Recruiting

A Phase 3 Study of NTLA-2001 in ATTRv-PN

NCT06672237

Conditions
Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, +23 more
Locations
  • Hospital Británico de Buenos Aires Buenos Aires, Argentina
  • Hospital Italiano de Buenos Aires (HIBA) Buenos Aires, Argentina
  • Hospital El Cruce San Juan Bautista, Argentina
  • Hospital das Clinicas da Universidade Estadual de Campinas (UNICAMP) Campinas, Brazil
View all 14 locations
View Trial Details
Completed

An Open-label Extension Study to Assess the Long-term Safety and Efficacy of ISIS 301012 (Mipomersen) in Patients With Familial Hypercholesterolemia or Severe-Hypercholesterolemia

NCT00694109

Conditions
Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, +14 more
Locations
  • Mission Viejo, California, United States
  • Newport Beach, California, United States
  • Bridgeport, Connecticut, United States
  • Melbourne, Florida, United States
View all 33 locations
View Trial Details

Related conditions