NCT01556516
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
- O&O Alpan Fairfax, Virginia, United States
Clinical trial condition
Lysosomal Storage Diseases, Nervous System
Explore clinical trials studying Lysosomal Storage Diseases, Nervous System. Study availability and eligibility vary by location and protocol.
513 public trials
105 recruiting studies
Lysosomal Storage Diseases, Nervous System trial results
Completed
An Open-Label, Dose Escalation Study to Evaluate the Safety and the Pharmacokinetics of Oral PRX-112
NCT02107846
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
- Locations
-
- Shaare Zedek Medical Center Jerusalem, Israel
NCT00001416
- Conditions
- Bone Diseases, Brain Diseases, Brain Diseases, Metabolic, +17 more
- Locations
-
- National Institute of Neurological Disorders and Stroke (NINDS) Bethesda, Maryland, United States
NCT02405598
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
- National Taiwan University Hospital Taipei, Taiwan
NCT02904395
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
Not specified
NCT02903654
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
Not specified
NCT00701415
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Decatur, Georgia, United States
- Cincinnati, Ohio, United States
- Seattle, Washington, United States
- Buenos Aires, Argentina
NCT01653444
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Asan Medical Center Songpa-gu, Seoul, South Korea
- Soon Cung Hyang University Hospital Yongsan-gu, Seoul, South Korea
- Ajou University School of Medicine Yeongtong-gu, Suwon, South Korea
Completed
Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
NCT00730314
- Conditions
- Agranulocytosis, Albinism, Anemia, +77 more
- Locations
-
- Children Hospital Los Angeles Los Angeles, California, United States
NCT00418847
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more
- Locations
-
- The Hospital for Sick Children Toronto, Ontario, Canada