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Clinical trial condition

Lysosomal Storage Diseases, Nervous System

Explore clinical trials studying Lysosomal Storage Diseases, Nervous System. Study availability and eligibility vary by location and protocol.

512 public trials 105 recruiting studies
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Lysosomal Storage Diseases, Nervous System trial results

Recruiting

Pompe Disease Registry Protocol

NCT00231400

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
Locations
  • University of Alabama at Birmingham- Site Number : 840106 Birmingham, Alabama, United States
  • Barrow Neurological Institute- Site Number : 840087 Phoenix, Arizona, United States
  • Phoenix Children's Hospital- Site Number : 840003 Phoenix, Arizona, United States
  • University of Arizona- Site Number : 840015 Tucson, Arizona, United States
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Recruiting

A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease

NCT07399704

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +23 more
Locations
  • Associação Hospitalar de Prot à Infância Dr. Raul Carneiro Água Verde, Curitiba, Brazil
  • Hospital de Clinicas de Porto Alegre Porto Alegre, Rio Grande do Sul, Brazil
  • Instituto Nacional de Saúde da Mulher, da Criança e do Adolescente Fernandes Figueira Rio de Janeiro, Brazil
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Recruiting

Pompe Pregnancy Sub-Registry

NCT00567073

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Barrow Neurol Group- Site Number : 840087 Phoenix, Arizona, United States
  • University of Florida Pediatrics Genetics- Site Number : 157138 Jacksonville, Florida, United States
  • Emory University School Of Medicine- Site Number : 840060 Atlanta, Georgia, United States
  • Indianapolis University School of Medicine- Site Number : 840027 Indianapolis, Indiana, United States
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Recruiting

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

NCT00358943

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +17 more
Locations
  • Phoenix Children's Hospital- Site Number : 840003 Phoenix, Arizona, United States
  • University of Arizona- Site Number : 840015 Tucson, Arizona, United States
  • Arkansas Children's Hospital- Site Number : 840109 Little Rock, Arkansas, United States
  • University of Arkansas for Medical Sciences- Site Number : 840113 Little Rock, Arkansas, United States
View all 318 locations
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