Skip to main content
OpenTrials

Clinical trial condition

Lysosomal Storage Diseases, Nervous System

Explore clinical trials studying Lysosomal Storage Diseases, Nervous System. Study availability and eligibility vary by location and protocol.

513 public trials 105 recruiting studies
Refine in advanced search Browse all conditions

Lysosomal Storage Diseases, Nervous System trial results

Completed

This Study is Designed to Evaluate PD/PK and Safety of Replagal Manufactured by Two Different Processes.

NCT01304277

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of Alberta Hospital Edmonton, Alberta, Canada
  • Queen Elizabeth II Health Sciences Centre Halifax, Nova Scotia, Canada
  • The Hospital for Sick Children Toronto, Ontario, Canada
  • INC Research Toronto, Ontario, Canada
View Trial Details
Completed

Alglucosidase Alfa Pompe Safety Sub-Registry

NCT01710813

Conditions
Anaphylaxis, Brain Diseases, Brain Diseases, Metabolic, +17 more
Locations
  • Investigational Site Number 840016 Phoenix, Arizona, United States
  • Investigational Site Number 840002 Durham, North Carolina, United States
  • Investigational Site Number 840004 Hershey, Pennsylvania, United States
  • Investigational Site Number 840014 Pittsburgh, Pennsylvania, United States
View all 18 locations
View Trial Details
Completed

A Study of Gene-Activated® Human Glucocerebrosidase (GA-GCB) Enzyme Replacement Therapy in Gaucher Disease

NCT00430625

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Hipolito Yrigoyen Buenos Aires, Argentina
  • Shaare Zedek Medical Center Jerusalem, Israel
  • Sociedad Espanola de Socorros Mutuos Asunción, Paraguay
  • National Research Center for Haematology Moscow, Russia
View Trial Details
Completed

Multicenter Study of HGT-1110 Administered Intrathecally in Children With Metachromatic Leukodystrophy (MLD)

NCT01510028

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • The Children's Hospital at Westmead Westmead, Australia
  • Rigshospitalet Copenhagen, Denmark
  • Hopital de Bicetre Le Kremlin-Bicêtre, Île-de-France Region, France
  • Center for Pediatric Clinical Studies Tübingen, Baden-Wurttemberg, Germany
View Trial Details
Completed

Multicenter Extension Study of Velaglucerase Alfa in Japanese Patients With Gaucher Disease

NCT01842841

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • Hamamatsu University School of Medicine Hamamatsu, Shizuoka, Japan
  • Iwata City Hospital Ōkubo, Shizuoka, Japan
  • The Jikei University School of Medicine Minato-ku, Tokyo, Japan
  • Chiba Children's Hospital Chiba, Japan
View Trial Details

Related conditions