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Clinical trial condition

Lysosomal Storage Diseases, Nervous System

Explore clinical trials studying Lysosomal Storage Diseases, Nervous System. Study availability and eligibility vary by location and protocol.

513 public trials 105 recruiting studies
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Lysosomal Storage Diseases, Nervous System trial results

Completed

Prophylactic Ranibizumab for Exudative Age-related Macular Degeneration

NCT02140151

Conditions
Age-Related Macular Degeneration, Brain Diseases, Brain Diseases, Metabolic, +18 more
Locations
  • Northern California Retina Vitreous Associates Mountain View, California, United States
  • Southern California Desert Retina Consultants Palm Desert, California, United States
  • Elman Retina Baltimore, Maryland, United States
  • Black Hills Regional Eye Institute Rapid City, South Dakota, United States
View Trial Details
Completed

Pharmacokinetics of Alglucosidase Alfa in Patients With Pompe Disease

NCT01410890

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • Investigational Site Number 840008 Valhalla, New York, United States
  • Investigational Site Number 840007 Cincinnati, Ohio, United States
  • Investigational Site Number 840005 Salt Lake City, Utah, United States
  • Investigational Site Number 840003 Fairfax, Virginia, United States
View Trial Details
Completed

Safety, Tolerability, PK, and Efficacy Evaluation of Repeat Ascending Doses of Olipudase Alfa in Pediatric Patients <18 Years of Age With Acid Sphingomyelinase Deficiency

NCT02292654

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • Investigational Site Number 840001 New York, United States
  • Investigational Site Number 076001 Porto Alegre, Brazil
  • Investigational Site Number 250002 Bron, France
  • Investigational Site Number 276001 Mainz, Germany
View Trial Details
Completed

Study of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher Disease

NCT02574286

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • Cedars Sinai Medical Center Beverly Hills, California, United States
  • Kaiser Permanente Los Angeles, California, United States
  • Emory Genetics Atlanta, Georgia, United States
  • Ann and Robert H Lurie Childrens Hospital of Chicago Chicago, Illinois, United States
View all 15 locations
View Trial Details

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