NCT02583672
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- University of Minnesota Minneapolis, Minnesota, United States
- New York University New York, United States
Clinical trial condition
Lysosomal Storage Diseases, Nervous System
Explore clinical trials studying Lysosomal Storage Diseases, Nervous System. Study availability and eligibility vary by location and protocol.
513 public trials
105 recruiting studies
Lysosomal Storage Diseases, Nervous System trial results
NCT04049760
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- University of South Florida Tampa, Florida, United States
- The Emory Clinic Atlanta, Georgia, United States
- University of Minnesota Masonic Children's Hospital and Clinics Minneapolis, Minnesota, United States
- Cincinnati Children's Hospital Cincinnati, Ohio, United States
NCT04281537
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Amicus Therapeutics, Inc. Philadelphia, Pennsylvania, United States
- Instituto de Genética e Erros Inatos do Metabolismo (IGEIM) São Paulo, Brazil
- Keio University Hospital Tokyo, Japan
- Yokohama Municipal Citizen's Hospital Yokohama, Japan
Completed
Study of IV VTS-270 for Infantile Liver Disease Associated With Niemann-Pick Disease, Type C
NCT03471143
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- St. Louis Children's Hospital St Louis, Missouri, United States
NCT01560182
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy
NCT01325025
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Unité de recherche biomédicale, Neurospin, I2BM / DSV / SAC/ CEA, Gif-sur-Yvette, France
- Service de Neurologie Pédiatrique, Hôpital Bicêtre Paris, France
- Bâtiment Lavoisier - Unité INSERM U 663,Hôpital Necker Enfants Malades Paris, France
NCT02699190
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
-
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
NCT04041102
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland Oakland, California, United States
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
- Hospital de Clínicas de Porto Alegre Porto Alegre, Brazil
- Montreal Children's Hospital Research Institute - McGill University Montreal, Quebec, Canada
NCT02675465
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
- Neuromuscular Research Centre Phoenix, Arizona, United States
- University of California Irvine Orange, California, United States
- University of Florida Gainesville, Florida, United States
- Emory University Division of Medical Genetics Decatur, Georgia, United States
Completed
A Prospective Study to Investigate Safety and Tolerability of Shorter Infusion of Fabrazyme
NCT06019728
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- UCLA Medical Center Site Number : 1003 Santa Monica, California, United States
- Emory University School of Medicine Site Number : 1005 Atlanta, Georgia, United States
- Infusion Associates Site Number : 1001 Grand Rapids, Michigan, United States
- Metropolitan Hospital Center Site Number : 1004 New York, United States