- Conditions
- Anderson-Fabry Disease, Aortic Stenosis, Subvalvular, Aortic Valve Disease, +67 more
- Locations
-
- IRCCS San Raffaele Scientific Institute Milan, Milano, Italy
Clinical trial condition
Lysosomal Storage Diseases, Nervous System
Explore clinical trials studying Lysosomal Storage Diseases, Nervous System. Study availability and eligibility vary by location and protocol.
520 public trials
102 recruiting studies
Lysosomal Storage Diseases, Nervous System trial results
NCT03240653
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
-
- Birmingham Childrens Hospital Birmingham, United Kingdom
- New Queen Elizabeth Hospital Birmingham, United Kingdom
- Cambridge University Hospital Cambridge, United Kingdom
- Great Ormond Street Hospital London, United Kingdom
Recruiting
Evaluate the Safety and Efficacy of Fabagal® (Agalsidase Beta) in Patients With Fabry Disease
NCT06081062
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Philippine General Hospital Manila, Philippines
- St.Luke's Medical Center Manila, Philippines
- Seoul Asan Center Seoul, Songpa-gu, South Korea
NCT06207552
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Children's Hospital of Fudan University Shanghai, China
Recruiting
Natural History of Pompe Disease
NCT03564561
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
- Hôpital Raymond Poincaré Garches, Hauts-de-Seine, France
NCT06272149
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- Xinhua Hospital Affiliated to Shanghai Jiao Tong University School of Medicine Shanghai, Shanghai Municipality, China
NCT00455104
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Alberta Children's Hospital Calgary, Alberta, Canada
- Vancouver General Hospital Adult Metabolic Diseases Clinic Vancouver, British Columbia, Canada
- Queen Elizabeth II Health Sciences Centre Halifax, Nova Scotia, Canada
- Toronto Western Hospital Toronto, Ontario, Canada
Recruiting
Biomarkers and Cardiac Imaging Diagnostic Assay for Monitoring Patients With Fabry Disease
NCT05698901
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +23 more
- Locations
-
- Charles Jia-Yin Hou Taipei, Taiwan
Recruiting
National Registry of Rare Kidney Diseases
NCT06065852
- Conditions
- AH Amyloidosis, AHL Amyloidosis, AL Amyloidosis, +207 more
- Locations
-
- Zoe Plummer Bristol, South West, United Kingdom
NCT05768035
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +25 more
- Locations
-
- Institut Paoli Calmettes Marseille, France
- Centre hospitalier universitaire de Nantes Nantes, France
- Hôpital Saint-Louis Paris, France
- CHU Toulouse- Institut Universitaire du cancer Toulouse- Oncopole Toulouse, France