Terminated
A Fabry Disease Gene Therapy Study
NCT04040049
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
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- Kaiser Permanente Los Angeles, California, United States
- Columbia University New York, United States
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
- Lysosomal and Rare Disorders Research and Treatment Center Fairfax, Virginia, United States