NCT03392987
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy
Clinical trial condition
Lysosomal Storage Disease
Explore clinical trials studying Lysosomal Storage Disease. Study availability and eligibility vary by location and protocol.
8 public trials
0 recruiting studies
Lysosomal Storage Disease trial results
NCT01560182
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy
NCT01626092
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +50 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
NCT00001671
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Lysosomal Storage Disease, +4 more
- Locations
-
- University of California, San Francisco San Francisco, California, United States
- Childrens National Medical Center Washington D.C., District of Columbia, United States
- Institut National de la Sante' et de la Recherche Medicale Clermont-Ferrand, Cedex, France
- Tel Aviv University Tel Aviv, Israel
NCT00852358
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Cognition Disorders, Cognitive Decline, +17 more
- Locations
-
- Children's Hospital & Research Center Oakland Oakland, California, United States
- Los Angeles Biomedical Institute at Harbor-UCLA Torrance, California, United States
- University of Minnesota Minneapolis, Minnesota, United States
NCT00744692
- Conditions
- Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +43 more
- Locations
-
- Duke University Medical Center Pediatric Blood and Marrow Transplant Program Durham, North Carolina, United States
NCT00001780
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Demyelinating Disease, +15 more
- Locations
-
- National Institute of Neurological Disorders and Stroke (NINDS) Bethesda, Maryland, United States
NCT00046202
- Conditions
- Cholesterol Metabolism, Congenital Hemidysplasia with Ichthyosiform Erythroderma and Limb Defects, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +8 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States