Lysosomal Storage Disease

Explore clinical trials studying Lysosomal Storage Disease. Study availability and eligibility vary by location and protocol.

8 public trials 0 recruiting studies

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Lysosomal Storage Disease trial results

Completed

NCT00046202

Conditions: Cholesterol Metabolism, Congenital Hemidysplasia with Ichthyosiform Erythroderma and Limb Defects, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +8 more
Locations: National Institutes of Health Clinical Center Bethesda, Maryland, United States

Completed

NCT03392987

Conditions: Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations: Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy

Completed

NCT01560182

Conditions: Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations: Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy

Completed

NCT01626092

Conditions: Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +50 more
Locations: Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States

Completed

NCT00001671

Conditions: Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Lysosomal Storage Disease, +4 more
Locations: University of California, San Francisco San Francisco, California, United States

Childrens National Medical Center Washington D.C., District of Columbia, United States

Institut National de la Sante' et de la Recherche Medicale Clermont-Ferrand, Cedex, France

Tel Aviv University Tel Aviv, Israel

Completed

NCT00852358

Conditions: Carbohydrate Metabolism, Inborn Errors, Cognition Disorders, Cognitive Decline, +17 more
Locations: Children's Hospital & Research Center Oakland Oakland, California, United States

Los Angeles Biomedical Institute at Harbor-UCLA Torrance, California, United States

University of Minnesota Minneapolis, Minnesota, United States

Completed

NCT00744692

Conditions: Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +43 more
Locations: Duke University Medical Center Pediatric Blood and Marrow Transplant Program Durham, North Carolina, United States

Completed

NCT00001780

Conditions: Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Demyelinating Disease, +15 more
Locations: National Institute of Neurological Disorders and Stroke (NINDS) Bethesda, Maryland, United States