Completed
Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C
NCT01344798
- Conditions
- Disease Attributes, Gamma-sarcoglycanopathy, Limb Girdle Muscular Dystrophy Type 2C, +6 more
- Locations
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- Hôpital Pitié-Salpêtrière Paris, France