Enrolling by Invitation
Strimvelis Registry Study to Follow-up Patients With Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID)
NCT03478670
- Conditions
- Immune System Diseases, Immunologic Deficiency Syndromes, Severe combined immunodeficiency due to adenosine deaminase deficiency
- Locations
-
- Ospedale San Raffaele Milan, Lombardy, Italy