Recruiting
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
NCT05040178
- Conditions
- Amino Acid Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
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- Children's National Hospital Washington D.C., District of Columbia, United States
- University of South Florida Tampa, Florida, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Riley Children's Hospital Indianapolis, Indiana, United States