Skip to main content
OpenTrials

Clinical trial condition

Hemoglobinopathies

Explore clinical trials studying Hemoglobinopathies. Study availability and eligibility vary by location and protocol.

80 public trials 23 recruiting studies
Refine in advanced search Browse all conditions

Hemoglobinopathies trial results

Completed

A Safety and Efficacy Study Evaluating CTX001 in Subjects With Severe Sickle Cell Disease

NCT03745287

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
Locations
  • Lucile Packard Children's Hospital of Stanford University Palo Alto, California, United States
  • Ann & Robert Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • University of Illinois at Chicago Hospitals and Health Systems Chicago, Illinois, United States
  • Columbia University Medical Center (21+ years) New York, United States
View all 17 locations
View Trial Details
Completed

Study of Efficacy, Safety and Tolerability of ACZ885 (Canakinumab) in Pediatric and Young Adult Patients With Sickle Cell Anemia

NCT02961218

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +7 more
Locations
  • Novartis Investigative Site Atlanta, Georgia, United States
  • Novartis Investigative Site Augusta, Georgia, United States
  • Novartis Investigative Site Greenville, North Carolina, United States
  • Novartis Investigative Site Toronto, Ontario, Canada
View all 15 locations
View Trial Details
Completed

A Safety and Efficacy Study Evaluating CTX001 in Participants With Transfusion-Dependent β-Thalassemia

NCT03655678

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
Locations
  • Lucile Packard Children's Hospital Palo Alto, California, United States
  • Ann & Robert Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • Columbia University Medical Center (21+ years) New York, United States
  • Columbia University Medical Center New York, United States
View all 14 locations
View Trial Details
Completed

A Study of Etavopivat in Patients With Thalassemia or Sickle Cell Disease

NCT04987489

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +15 more
Locations
  • TOI Clinical Research Cerritos, California, United States
  • [Legal] Children's Hospital Los Angeles Los Angeles, California, United States
  • University of Californ LA-UCLA Los Angeles, California, United States
  • UCSF Oakland Benioff ChildHosp Oakland, California, United States
View all 32 locations
View Trial Details
Completed

Treosulfan-based Versus Busulfan-based Conditioning in Paediatric Patients With Non-malignant Diseases

NCT02349906

Conditions
Bone Marrow Diseases, Bone Marrow Failure Disorders, Bone Marrow Failure Syndromes, +11 more
Locations
  • University Hospital Motol, Dep. of Paediatric Haematology and Oncology Prague, Czechia
  • Department of Pediatric Oncology & Hematology, Charite Berlin Berlin, Germany
  • University Children's Hospital Essen Pediatric stem cell transplantation Essen, Germany
  • University Hospital Frankfurt Frankfurt am Main, Germany
View all 21 locations
View Trial Details

Related conditions