Active, Not Recruiting
Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)
NCT05356195
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
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- TriStar Medical Group Children's Specialists - Pediatric Oncology Nashville, Tennessee, United States
- Hospital for Sick Children - Hematology Toronto, Canada
- University Hospital Dusseldorf - Department of Pediatric Oncology, Hematology and Clinical Immunology Düsseldorf, Germany
- IRCSS Ospedale Pediatrico Bambino Gesu - Dipartimento di Onco-Ematologia e Terapia Cellulare e Genica Rome, Italy