NCT00158600
- Conditions
- Acid Maltase Deficiency Disease, Brain Diseases, Brain Diseases, Metabolic, +16 more
- Locations
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- Tower Hematology Oncology Medical Group Beverly Hills, California, United States
- Children's National Medical Center Washington D.C., District of Columbia, United States
- Washington University Medical Center St Louis, Missouri, United States
- Mount Sinai School of Medicine New York, United States