Completed
Safety and Efficacy Evaluation of Repeat neoGAA Dosing in Late Onset Pompe Disease Patients.
NCT01898364
- Conditions
- Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +15 more
- Locations
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- Investigational Site Number 840006 Phoenix, Arizona, United States
- Investigational Site Number 840010 Jacksonville, Florida, United States
- Investigational Site Number 840001 Kansas City, Kansas, United States
- Investigational Site Number 840008 St Louis, Missouri, United States