Active, Not Recruiting
Avalglucosidase Alfa French Post-trial Access for Participants With Pompe Disease (PTA Avalglucosidase)
NCT05164055
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +12 more
- Locations
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- Investigational Site Number : 2500004 Bordeaux, France
- Investigational Site Number : 2500005 Brest, France
- Investigational Site Number : 2500008 Clermont-Ferrand, France
- Investigational Site Number : 2500009 Lille, France