Active, Not Recruiting
A Phase 1/2/3 Study of TSHA-102 Gene Therapy in Females With Rett Syndrome (REVEAL Pivotal Study)
NCT05606614
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +12 more
- Locations
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- City of Hope Duarte, California, United States
- UC San Diego La Jolla, California, United States
- UC San Francisco Benioff Children's Hospital Oakland, California, United States
- Rush University Medical Center Chicago, Illinois, United States