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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

449 public trials 107 recruiting studies

Genetic Diseases, Inborn trial results

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystic Fibrosis, Digestive System Diseases, +7 more
Locations
  • Children's Hospital of Colorado Aurora, Colorado, United States
  • Riley Hospital for Children Indianapolis, Indiana, United States
  • Washington University School of Medicine St Louis, Missouri, United States
  • University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
View all 25 locations
Conditions
Anxiety Disorders, Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, +16 more
Locations
  • Swedish Orphan Biovitrum Research Site Copenhagen, Denmark
  • Swedish Orphan Biovitrum Research Site Helsinki, Finland
  • Swedish Orphan Biovitrum Research Site Gothenburg, Sweden
  • Swedish Orphan Biovitrum Research Site Malmö, Sweden
Conditions
Blood Protein Disorders, Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +19 more
Locations
  • Arkansas Cancer Research Center Little Rock, Arkansas, United States
  • University of Arkansas for Medical Sciences Little Rock, Arkansas, United States
  • Medicine Branch Bethesda, Maryland, United States
Conditions
Adeno-Associated Virus (AAV), Blood Coagulation Disorder, Blood Coagulation Disorders, +18 more
Locations
  • Orthopaedic Institute for Children Los Angeles, California, United States
  • Illinois Bleeding and Clotting Disorders Institute Peoria, Illinois, United States
  • University of Michigan Ann Arbor, Michigan, United States
  • Mississippi Center for Advanced Medicine Madison, Mississippi, United States