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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,537 public trials 2,139 recruiting studies
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Genetic Diseases, Inborn trial results

Recruiting

A Study to Evaluate the Safety and Tolerability of TOS-358 in Women With HR+ HER2- Breast Cancer

NCT05683418

Conditions
Breast Diseases, Breast Neoplasms, Congenital Abnormalities, +15 more
Locations
  • Northwestern Memorial Hospital Chicago, Illinois, United States
  • Beth Israel Deaconess Medical Center Boston, Massachusetts, United States
  • Dana-Farber Cancer Institute Boston, Massachusetts, United States
  • Comprehensive Cancer Centers of Nevada Las Vegas, Nevada, United States
View all 18 locations
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Recruiting

ATHNdataset Registry

NCT06820515

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +33 more
Locations
  • American Thrombosis and Hemostasis Network Hickory, North Carolina, United States
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Recruiting

A Study of Bleeding and Treatment in Participants With Von Willebrand Disease

NCT06610201

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Blood Platelet Disorders, +16 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Children's Hospital of Los Angeles Los Angeles, California, United States
  • University of Miami Hospital and Clinics, Sylvester Comprehensive Cancer Center Miami, Florida, United States
View all 17 locations
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Recruiting

A Clinical Trial to Evaluate Efficacy and Safety of Navepegritide in Adolescents (12 - 18 Years of Age) With Achondroplasia.

NCT06732895

Conditions
Achondroplasia, Bone Diseases, Bone Diseases, Developmental, +5 more
Locations
  • Ascendis Investigational Site Montreal, Canada
  • Ascendis Investigational Site Copenhagen, Denmark
  • Ascendis Investigational Site Paris, France
  • Ascendis Investigational Site Dublin, Ireland
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Recruiting

Phase 2/3 Clinical Study of QRX003 Lotion in Subjects With Netherton Syndrome

NCT07538583

Conditions
Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
Locations
  • Center for Dermatology Clinical Research Fremont, California, United States
  • Yale University School of Medicine New Haven, Connecticut, United States
  • Dawes Fretzin Clinical Reseacrh Group Indianapolis, Indiana, United States
  • Beacon Clinical Research Quincy, Massachusetts, United States
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