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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,656 public trials 2,147 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

A Long-term Treatment With B-VEC for Dystrophic Epidermolysis Bullosa

NCT04917874

Conditions
Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
Locations
  • Mission Dermatology Center Rancho Santa Margarita, California, United States
  • Stanford University Redwood City, California, United States
  • Pediatric Skin Research Coral Gables, Florida, United States
  • Northwestern University Chicago, Illinois, United States
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Completed

Study of Trofinetide for the Treatment of Girls and Women With Rett Syndrome (LAVENDER™)

NCT04181723

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • Translational Gemomics Research Institute (TGen) Phoenix, Arizona, United States
  • University of California, San Diego La Jolla, California, United States
  • UC Davis MIND Institute Sacramento, California, United States
View all 21 locations
View Trial Details
Completed

Carisbamate Safety Study in Adult and Pediatric Subjects With Lennox-Gastaut Syndrome

NCT04062981

Conditions
Brain Diseases, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +5 more
Locations
  • Johns Hopkins Hospital Baltimore, Maryland, United States
  • Dartmouth-Hitchcock Medical Center Lebanon, New Hampshire, United States
  • Oregon Health and Science University Portland, Oregon, United States
  • The University of Utah School of Medicine - Primary Children's Hospital (Primary Children's Medical Center) Salt Lake City, Utah, United States
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