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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,648 public trials 2,153 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

Study to Assess Efficacy and Safety of VIT-2763 (Vamifeport) in Subjects With Sickle Cell Disease

NCT04817670

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +7 more
Locations
  • Investigator Site 709 Birmingham, Alabama, United States
  • Investigator Site 708 Los Angeles, California, United States
  • Investigator Site 713 Aurora, Colorado, United States
  • Investigator Site 706 Hollywood, Florida, United States
View all 22 locations
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Completed

A Study to Learn How Well the Study Treatment Zabedosertib (BAY1834845) Works and How Safe it is Compared to Placebo in Adult Participants With Moderate-to-severe Atopic Dermatitis

NCT05656911

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • NorthShore University HealthSystem | Skokie Hospital - Dermatology Department Skokie, Illinois, United States
  • Beth Israel Deaconess Medical Center - Dermatology Boston, Massachusetts, United States
  • University of Cincinnati College of Medicine - Dermatology Cincinnati, Ohio, United States
  • Arlington Research Center, Inc. | Arlington, TX Arlington, Texas, United States
View all 22 locations
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Completed

A Study of Lumasiran in Infants and Young Children With Primary Hyperoxaluria Type 1

NCT03905694

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, +14 more
Locations
  • Clinical Trial Site Rochester, Minnesota, United States
  • Clinical Trial Site Houston, Texas, United States
  • Clinical Trial Site Lyon, France
  • Clinical Trial Site Paris, France
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Completed

A Study to Evaluate Adverse Events and Change in Disease Activity Comparing Oral Upadacitinib to Subcutaneous Dupilumab in Adolescent and Adult Participants With Moderate to Severe Atopic Dermatitis

NCT05601882

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • Medical Dermatology Specialists /ID# 250212 Phoenix, Arizona, United States
  • Alliance Dermatology and Mohs Center /ID# 249671 Phoenix, Arizona, United States
  • Clinical Trials Institute - Northwest Arkansas /ID# 249838 Fayetteville, Arkansas, United States
  • Arkansas Research Trials /ID# 250722 North Little Rock, Arkansas, United States
View all 257 locations
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Completed

COVID-19 Vaccine Response in Sickle Cell Disease

NCT05139992

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +19 more
Locations
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
  • Johns Hopkins University Baltimore, Maryland, United States
  • Montefiore Hospital The Bronx, New York, United States
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