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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,619 public trials 2,162 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

A Study Assessing Rocatinlimab (AMG 451) Monotherapy in Moderate-to-severe Atopic Dermatitis (AD) (ROCKET-Horizon)

NCT05651711

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +10 more
Locations
  • Research Solutions of Arizona, PC Litchfield Park, Arizona, United States
  • Center for Dermatology and Plastic Surgery Scottsdale, Arizona, United States
  • Clinical Trials Institute of Northwest Arkansas Fayetteville, Arkansas, United States
  • Burke Pharmaceutical Research Hot Springs, Arkansas, United States
View all 197 locations
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Completed

Effect of Evolocumab in Patients at High Cardiovascular Risk Without Prior Myocardial Infarction or Stroke

NCT03872401

Conditions
Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Coronary Disease, +13 more
Locations
  • North Alabama Research Center LLC Athens, Alabama, United States
  • Cardiovascular Associates Birmingham, Alabama, United States
  • Heart Center Research LLC Huntsville, Alabama, United States
  • Mobile Heart Specialists PC Mobile, Alabama, United States
View all 852 locations
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Completed

A Double-Blind, Active-Controlled, Multiple-Ascending Dose Study of Aerosolized RSP-1502 in Subjects With CF and Chronic PA Lung Infection

NCT06016088

Conditions
Bacterial Infections, Bacterial Infections and Mycoses, Bronchial Diseases, +27 more
Locations
  • Tucson Cystic Fibrosis Center Tucson, Arizona, United States
  • Center for Cystic Fibrosis at Keck Medical Center of USC Los Angeles, California, United States
  • Stanford University Medical Center Palo Alto, California, United States
  • Augusta University Augusta, Georgia, United States
View all 22 locations
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Completed

Pharmacokinetics, Safety and Efficacy of Nemolizumab in Participants With Moderate-to-Severe Atopic Dermatitis

NCT04921345

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, Dermatitis, Atopic, +9 more
Locations
  • Galderma Investigational Site #8636 Fountain Valley, California, United States
  • Galderma Investigational Site #9937 San Diego, California, United States
  • Galderma Investigational Site #9930 Vista, California, United States
  • Galderma Investigational Site #9929 Coral Gables, Florida, United States
View all 23 locations
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Completed

Pharmacokinetic Comparison of Efanesoctocog Alfa vs Other EHL-rFVIII Products in Participants With Severe Haemophilia A

NCT06579144

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +6 more
Locations
  • Sobi Investigational Site Sofia, Bulgaria
  • Sobi Investigational Site Bonn, Germany
  • Sobi Investigational site Frankfurt, Germany
  • Sobi Investigational Site Milan, Italy
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Completed

A Safety, Tolerability and Pharmacokinetics Study of VRDN-003 in Participants With Thyroid Eye Disease (TED)

NCT07155668

Conditions
Autoimmune Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Endocrine System Diseases, +12 more
Locations
  • United Medical Research Institute Inglewood, California, United States
  • C&A Clinical Trials Corp Cape Coral, Florida, United States
  • Ilumina Medical Research Kissimmee, Florida, United States
  • Med-Care Research Miami, Florida, United States
View all 13 locations
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