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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,619 public trials 2,162 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

Hormonal Regulation of Puberty and Fertility

NCT01511588

Conditions
Adolescents, Amenorrhea, Congenital Abnormalities, +20 more
Locations
  • National Institutes of Health Clinical Center Bethesda, Maryland, United States
  • NIEHS Clinical Research Unit (CRU) Research Triangle Park, North Carolina, United States
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Completed

A Study Evaluating Physical Activity and Joint Health in Severe Haemophilia A Patients ≥12 Years Treated Once Weekly With Efanesoctocog Alfa

NCT05817812

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Investigational Site Vienna, Austria
  • Investigational Site Zagreb, Croatia
  • Investigational Site Brno, Czechia
  • Investigational Site Prague, Czechia
View all 30 locations
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Completed

A Study to Learn How Safe the Study Treatment BAY94-9027 is and How it Affects the Body in Previously Treated Children Aged 7 to Less Than 12 Years With Severe Hemophilia A, a Genetic Bleeding Disorder That is Caused by the Lack of a Protein Called Clotting Factor 8 (FVIII) in the Blood

NCT05147662

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Children, +9 more
Locations
  • Arnold Palmer Hospital for Children Orlando, Florida, United States
  • Hospital de Niños Sor María Ludovica La Plata, Buenos Aires, Argentina
  • Instituo Hematología Arbesú Godoy Cruz, Mendoza Province, Argentina
  • Instituto de Hematología Dr. Rubén Dávoli Rosario, Santa Fe Province, Argentina
View all 18 locations
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Completed

A Trial to Investigate the Non-inferiority of Pegloticase Administered Every 4 Weeks (Q4W) With MTX Compared With Every 2 Weeks (Q2W) With MTX in Participants With Uncontrolled Refractory Gout

NCT06229145

Conditions
Arthritis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Crystal Arthropathies, +9 more
Locations
  • The University of Alabama at Birmingham (UAB) Birmingham, Alabama, United States
  • Orthopedic Physicians Alaska - Rheumatology and Infusion Anchorage, Alaska, United States
  • Arizona Arthritis and Rheumatology Associates - Chandler Chandler, Arizona, United States
  • Arizona Arthritis and Rheumatology Rese Flagstaff, Arizona, United States
View all 74 locations
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