Skip to main content
OpenTrials

Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,619 public trials 2,162 recruiting studies
Refine in advanced search Browse all conditions

Genetic Diseases, Inborn trial results

Completed

Recombinant Fusion Protein Linking Coagulation Factor IX With Albumin (rIX-FP) in Chinese Subjects With Hemophilia B Previously Treated With FIX Therapy

NCT06399289

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Beijing Children's Hospital Beijing, Beijing Municipality, China
  • Union Hospital Affiliated to Fujian Medical University Fuzhou, Fujian, China
  • Nanfang Hospital of Southern Medical University Guangzhou, Guangdong, China
  • Affiliated Hospital of Guizhou Medical University Guiyang, Guizhou, China
View Trial Details
Completed

Phase 3, Randomized, Placebo-Controlled Study of Tinlarebant to Explore Safety and Efficacy in Adolescent Stargardt Disease

NCT05244304

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Eye Diseases, Hereditary, +6 more
Locations
  • Belite Study Site Palo Alto, California, United States
  • Belite Study Site Minneapolis, Minnesota, United States
  • Belite Study Site Salt Lake City, Utah, United States
  • Belite Study Site Westmead, New South Wales, Australia
View all 19 locations
View Trial Details
Completed

A Study Assessing Rocatinlimab on Vaccine Antibody Response in Moderate-to-severe Atopic Dermatitis (AD) (ROCKET - VOYAGER)

NCT05899816

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +10 more
Locations
  • Affiliated Dermatology Scottsdale, Arizona, United States
  • Center for Dermatology and Plastic Surgery Scottsdale, Arizona, United States
  • Scottsdale Clinical Trials Scottsdale, Arizona, United States
  • Medical Advancement Centers of Arizona Tempe, Arizona, United States
View all 85 locations
View Trial Details
Completed

A Study Evaluating Rocatinlimab in Moderate-to-severe Atopic Dermatitis (ROCKET-IGNITE)

NCT05398445

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • Cahaba Dermatology and Skin Health Center Birmingham, Alabama, United States
  • Alliance Dermatology and Mohs Center Phoenix, Arizona, United States
  • Anaheim Clinical Trials Anaheim, California, United States
  • First OC Dermatology Fountain Valley, California, United States
View all 202 locations
View Trial Details
Completed

A Study to Evaluate the Efficacy and Safety of Subcutaneous Amlitelimab Monotherapy Compared With Placebo in Participants Aged 12 Years and Older With Moderate-to-severe Atopic Dermatitis

NCT06130566

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, Dermatitis Atopic, +9 more
Locations
  • Scottsdale Clinical Trials- Site Number : 8401149 Scottsdale, Arizona, United States
  • First OC Dermatology- Site Number : 8401025 Fountain Valley, California, United States
  • Center for Dermatology Clinical Research- Site Number : 8401018 Fremont, California, United States
  • Sunwise Clinical Research- Site Number : 8401022 Lafayette, California, United States
View all 148 locations
View Trial Details
Completed

Research Study Investigating How Well NDec Works in People With Sickle Cell Disease

NCT05405114

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +7 more
Locations
  • University Of South Alabama Mobile, Alabama, United States
  • Keck Medical Center of USC - Outpatient Clinic Los Angeles, California, United States
  • UCSF Oakland Benioff ChildHosp Oakland, California, United States
  • Center for Inherited Blood Dis Orange, California, United States
View all 118 locations
View Trial Details
Completed

A Single-ascending Dose (Part A) and Repeat-dose (Part B) Study to Investigate the Safety, Pharmacokinetics and Efficacy (Part B Only) of UCB1381 in Healthy Study Participants (Part A) and in Study Participants With Moderate to Severe Atopic Dermatitis (Part B)

NCT05277571

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • Up0110 125 Beverly Hills, California, United States
  • Up0110 101 Glendale, California, United States
  • Up0110 116 Los Angeles, California, United States
  • Up0110 121 Northridge, California, United States
View all 16 locations
View Trial Details

Related conditions