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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,613 public trials 2,162 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

A Dose Escalation Trial Evaluating Safety, Efficacy, and Pharmacokinetics of Multiple Subcutaneous Doses of TransCon CNP Administered Once Weekly in Children With Achondroplasia

NCT05246033

Conditions
Achondroplasia, Bone Diseases, Bone Diseases, Developmental, +6 more
Locations
  • Ascendis Pharma Investigational Site Beijing, China
  • Ascendis Pharma Investigational Site Guangzhou, China
  • Ascendis Pharma Investigational Site Hangzhou, China
  • Ascendis Pharma Investigational Site Shanghai, China
View Trial Details
Completed

A Multicenter Study Assessing the Efficacy and Safety of STN1010904 Ophthalmic Suspension 0.03% and 0.1% Compared With Vehicle in Subjects With Fuchs Endothelial Corneal Dystrophy (FECD)

NCT05376176

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Corneal Diseases, Corneal Dystrophies, Hereditary, +5 more
Locations
  • Stein Eye Institution UCLA Los Angeles, California, United States
  • Price Vision Group Indianapolis, Indiana, United States
  • Johns Hopkins University Baltimore, Maryland, United States
  • Mayo Clinic Rochester, Minnesota, United States
View all 15 locations
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Completed

A Study of Enlicitide Decanoate (MK-0616 Oral PCSK9 Inhibitor) in Adults With Hypercholesterolemia (MK-0616-013) CORALreef Lipids

NCT05952856

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Familial Hypercholesterolemia, +10 more
Locations
  • Alliance for Multispecialty Research, LLC ( Site 0093) Daphne, Alabama, United States
  • G&L Research ( Site 0043) Foley, Alabama, United States
  • Synexus Clinical Research US, Inc.-Synexus Clinical Research US, Inc - Central Phoenix ( Site 0084) Phoenix, Arizona, United States
  • National Heart Institute-Research ( Site 0087) Beverly Hills, California, United States
View all 168 locations
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Completed

A Study Assessing Rocatinlimab in Combination With Topical Corticosteroid and/or Topical Calcineurin Inhibitors in Adult Participants With Moderate-to-severe Atopic Dermatitis (AD)

NCT05724199

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +10 more
Locations
  • The University of Alabama at Birmingham Birmingham, Alabama, United States
  • Medical Dermatology Specialists Phoenix, Arizona, United States
  • Southwest Skin Specialists Phoenix, Arizona, United States
  • US Dermatology Partners Sun City West Sun City West, Arizona, United States
View all 234 locations
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