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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,613 public trials 2,162 recruiting studies
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Genetic Diseases, Inborn trial results

Active, not recruiting

CAMPSIITE™ RGX-121 Gene Therapy in Subjects With MPS II (Hunter Syndrome)

NCT03566043

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
Locations
  • University of California San Francisco, Benioff Children's Hospital Oakland, California, United States
  • St. Peter's University Hospital New Brunswick, New Jersey, United States
  • Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
  • Children's Hospital of Pittsburgh - UPMC: Program for Neurodevelopment in Rare Disorders Pittsburgh, Pennsylvania, United States
View Trial Details
Active, not recruiting

Kidney Function in Sickle Cell Anemia

NCT03277547

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +20 more
Locations
  • University of North Carolina-Chapel Hill Chapel Hill, North Carolina, United States
  • Ohio State Adult Sickle Cell Program Columbus, Ohio, United States
  • UTHSC Center for Sickle Cell Disease Memphis, Tennessee, United States
View Trial Details
Active, not recruiting

Intestinal Inflammation in CF Patients

NCT04392544

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystic Fibrosis, Cystic Fibrosis Gastrointestinal Disease, +7 more
Locations
  • The Hospital for Sick Children Toronto, Ontario, Canada
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Active, not recruiting

Observatory of Patients With Haemophilia B Treated by IdElvion®

NCT05086575

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +8 more
Locations
  • CHU Amiens - Picardie Amiens, France
  • CH Annecy Genevois Annecy, France
  • CHRU Besançon Besançon, France
  • CHU Bordeaux - Hôpital Pellegrin Bordeaux, France
View all 28 locations
View Trial Details
Active, not recruiting

A Herbal Compound for Eczema

NCT06758752

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +13 more
Locations
  • Fasa university of medical sciences Fasa, Fars, Iran
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