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Genetic Diseases, Inborn

Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,603 public trials 2,158 recruiting studies

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Genetic Diseases, Inborn trial results

Active, not recruiting

Robotic vs Open Nephrectomy for ADPKD

NCT07355114

Conditions: Abnormalities, Multiple, Autosomal Dominant Polycystic Kidney Disease (ADPKD), Ciliopathies, +12 more
Locations: IRCSS Azienda Ospedaliero-Universitaria di Bologna Bologna, Bo, Italy

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Active, not recruiting

Interleukin-15 Armored Glypican 3-specific Chimeric Antigen Receptor Expressed in T Cells for Pediatric Solid Tumors

NCT04377932

Conditions: Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Digestive System Neoplasms, +32 more
Locations: Texas Children's Hospital Houston, Texas, United States

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Active, not recruiting

SAD of IVT PYC-001 in OPA1 Mutation-Associated Autosomal Dominant Optic Atrophy (Sundew)

NCT06461286

Conditions: Autosomal Dominant Optic Atrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, +16 more
Locations: Save Sight Institute - Sydney Eye Hospital Sydney, New South Wales, Australia

Center for Eye Research Australia (CERA) East Melbourne, Victoria, Australia

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Active, not recruiting

SGLT2 Inhibitor Therapy in Cystic Fibrosis-related Diabetes

NCT06149793

Conditions: Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystic Fibrosis, Cystic Fibrosis-related Diabetes, +6 more
Locations: University of Minnesota Minneapolis, Minnesota, United States

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Active, not recruiting

Randomized Controlled Trial of Alert-Based Computerized Decision Support for Optimizing Low-Density Lipoprotein Management

NCT05088759

Conditions: ASCVD, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, +11 more
Locations: Brigham and Women's Hospital Boston, Massachusetts, United States

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Active, not recruiting

Intrarenal Microvasculature in ADPKD

NCT05288998

Conditions: Abnormalities, Multiple, Autosomal Dominant Polycystic Kidney Disease, Ciliopathies, +12 more
Locations: Mayo Clinic Rochester, Minnesota, United States

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Active, not recruiting

A Study to Evaluate the Safety and Tolerability of RAG-18 in Pediatric Patients With Duchenne Muscular Dystrophy

NCT07282652

Conditions: Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
Locations: Peking Union Medical College Hospital Beijing, China

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Active, not recruiting

CHOICES3: Sickle Cell Disease Parenting CHOICES

NCT05292781

Conditions: Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
Locations: University of Florida Gainesville, Florida, United States

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Active, not recruiting

Evolution of the Functional and Muscular State of Patients With Muscular Dystrophy 2A Belts

NCT06390566

Conditions: Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb Girdle Muscular Dystrophy, +8 more
Locations: Hôpital Henri Mondor Créteil, Île-de-France Region, France

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Active, not recruiting

A Phase I Clinical Study of ER2001 Injection for the Treatment of Early Manifest Huntington's Disease.

NCT07339514

Conditions: Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +13 more
Locations: First Affiliated Hospital of Guangzhou Medical University Guangzhou, Guangdong, China

First Affiliated Hospital of Sun Yat-sen University Guangzhou, Guangdong, China

West China Hospital of Sichuan University Chengdu, Sichuan, China

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Genetic Diseases, Inborn

Genetic Diseases, Inborn trial results

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