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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,597 public trials 2,159 recruiting studies
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Genetic Diseases, Inborn trial results

Active, not recruiting

Strength and Muscle Related Outcomes for Nutrition and Lung Function in CF

NCT05639556

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystic Fibrosis, Digestive System Diseases, +5 more
Locations
  • University of Arizona Tucson, Arizona, United States
  • University of Arkansas for Medical Sciences (UAMS) Little Rock, Arkansas, United States
  • Emory Atlanta, Georgia, United States
  • Northwestern University Chicago, Illinois, United States
View all 23 locations
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Active, not recruiting

Evaluation of D-Fi for the Treatment of Wounds Due to DEB

NCT06892639

Conditions
Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
Locations
  • Stanford University School of Medicine, Dermatology Redwood City, California, United States
  • Mission Dermatology Santa Margarita, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • University of Massachusetts Worcester, Massachusetts, United States
View Trial Details
Active, not recruiting

PASS of Paediatric Patients Initiating Selumetinib

NCT05388370

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +14 more
Locations
  • Research Site Vienna, Austria
  • Research Site Amiens, France
  • Research Site Angers, France
  • Research Site Bordeaux, France
View all 46 locations
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Active, not recruiting

A Phase 2/3 Study to Evaluate the Efficacy and Safety of Tinlarebant in Subjects With Stargardt Disease

NCT06388083

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Eye Diseases, Hereditary, +7 more
Locations
  • Belite Study Site - US08 Phoenix, Arizona, United States
  • Belite Study Site - US05 La Jolla, California, United States
  • Belite Study Site - US09 San Francisco, California, United States
  • Belite Study Site - US06 Miami, Florida, United States
View all 18 locations
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Active, not recruiting

Efficacy and Safety of Gemlapodect (NOE-105) in Adults and Adolescents With Tourette Syndrome

NCT06315751

Conditions
Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +10 more
Locations
  • Noema TTS-201 Site #81 Sun City, Arizona, United States
  • Noema TTS-201 Site #95 Bellflower, California, United States
  • Noema TTS-201 Site #75 Glendale, California, United States
  • Noema TTS-201 Site #59 San Rafael, California, United States
View all 46 locations
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