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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,584 public trials 2,158 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

Combination Chemotherapy With or Without Radiation Therapy in Treating Young Patients With Newly Diagnosed Stage III or Stage IV Wilms' Tumor

NCT00379340

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, +16 more
Locations
  • Children's Hospital of Alabama Birmingham, Alabama, United States
  • University of Alabama at Birmingham Cancer Center Birmingham, Alabama, United States
  • USA Health Strada Patient Care Center Mobile, Alabama, United States
  • Phoenix Childrens Hospital Phoenix, Arizona, United States
View all 227 locations
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Completed

CureDuchenne Link®: A Resource for Research

NCT04972604

Conditions
Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, +9 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • CureDuchenne Newport Beach, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Rare Disease Research Atlanta, Georgia, United States
View Trial Details
Completed

A Study to Assess the Safety, Tolerability, and Efficacy of Rocatinlimab in Adolescent Participants With Moderate-to-severe Atopic Dermatitis (AD)

NCT05633355

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • Phoenix Childrens Hosptial Phoenix, Arizona, United States
  • Medical Advancement Centers of Arizona Tempe, Arizona, United States
  • Dermatology Trial Associates Bryant, Arkansas, United States
  • Little Rock Allergy and Asthma Clinical Research Center Little Rock, Arkansas, United States
View all 77 locations
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Completed

Safety Study in Subjects ≥ 12 Years of Age With Hereditary Angioedema Switching to Garadacimab

NCT06806657

Conditions
Angioedema, Angioedemas, Hereditary, Cardiovascular Diseases, +14 more
Locations
  • Research Solutions of Arizona Litchfield Park, Arizona, United States
  • Allergy and Asthma Clinic of Northwest Arkansas Bentonville, Arkansas, United States
  • Donald Levy M.D. Orange, California, United States
  • Raffi Tachdjian MD, Inc. Santa Monica, California, United States
View Trial Details
Completed

Recombinant Fusion Protein Linking Coagulation Factor IX With Albumin (rIX-FP) in Chinese Subjects With Hemophilia B Previously Treated With FIX Therapy

NCT06399289

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Beijing Children's Hospital Beijing, Beijing Municipality, China
  • Union Hospital Affiliated to Fujian Medical University Fuzhou, Fujian, China
  • Nanfang Hospital of Southern Medical University Guangzhou, Guangdong, China
  • Affiliated Hospital of Guizhou Medical University Guiyang, Guizhou, China
View Trial Details
Completed

Phase 3, Randomized, Placebo-Controlled Study of Tinlarebant to Explore Safety and Efficacy in Adolescent Stargardt Disease

NCT05244304

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Eye Diseases, Hereditary, +6 more
Locations
  • Belite Study Site Palo Alto, California, United States
  • Belite Study Site Minneapolis, Minnesota, United States
  • Belite Study Site Salt Lake City, Utah, United States
  • Belite Study Site Westmead, New South Wales, Australia
View all 19 locations
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Completed

A Study Assessing Rocatinlimab on Vaccine Antibody Response in Moderate-to-severe Atopic Dermatitis (AD) (ROCKET - VOYAGER)

NCT05899816

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +10 more
Locations
  • Affiliated Dermatology Scottsdale, Arizona, United States
  • Center for Dermatology and Plastic Surgery Scottsdale, Arizona, United States
  • Scottsdale Clinical Trials Scottsdale, Arizona, United States
  • Medical Advancement Centers of Arizona Tempe, Arizona, United States
View all 85 locations
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Completed

A Study Evaluating Rocatinlimab in Moderate-to-severe Atopic Dermatitis (ROCKET-IGNITE)

NCT05398445

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • Cahaba Dermatology and Skin Health Center Birmingham, Alabama, United States
  • Alliance Dermatology and Mohs Center Phoenix, Arizona, United States
  • Anaheim Clinical Trials Anaheim, California, United States
  • First OC Dermatology Fountain Valley, California, United States
View all 202 locations
View Trial Details

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