NCT05509569
- Conditions
- Angioedema, Angioedemas, Hereditary, Cardiovascular Diseases, +14 more
- Locations
-
- Takeda selected site Tokyo, Japan
Clinical trial condition
Genetic Diseases, Inborn
Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.
12,584 public trials
2,158 recruiting studies
Genetic Diseases, Inborn trial results
NCT05376176
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Corneal Diseases, Corneal Dystrophies, Hereditary, +5 more
- Locations
-
- Stein Eye Institution UCLA Los Angeles, California, United States
- Price Vision Group Indianapolis, Indiana, United States
- Johns Hopkins University Baltimore, Maryland, United States
- Mayo Clinic Rochester, Minnesota, United States
NCT00111384
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +18 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT03049475
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +11 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Completed
Study of Safety, PK, and Efficacy of Multiple Ascending Doses of HZBio1 in Patients With Gout
NCT07752810
- Conditions
- Arthritis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Crystal Arthropathies, +9 more
- Locations
-
- Huashan Hospital, Fudan University Shanghai, Shanghai Municipality, China
NCT06251843
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +7 more
- Locations
-
- Alder Hey Children's Hospital Liverpool, United Kingdom
- Guy's and St Thomas' NHS Foundation Trust London, United Kingdom
Completed
Stem Cell Gene Therapy for Cystinosis
NCT03897361
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Genetic Diseases, Inborn, +4 more
- Locations
-
- University of California San Diego La Jolla, California, United States
NCT05952856
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Familial Hypercholesterolemia, +10 more
- Locations
-
- Alliance for Multispecialty Research, LLC ( Site 0093) Daphne, Alabama, United States
- G&L Research ( Site 0043) Foley, Alabama, United States
- Synexus Clinical Research US, Inc.-Synexus Clinical Research US, Inc - Central Phoenix ( Site 0084) Phoenix, Arizona, United States
- National Heart Institute-Research ( Site 0087) Beverly Hills, California, United States
NCT05724199
- Conditions
- Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +10 more
- Locations
-
- The University of Alabama at Birmingham Birmingham, Alabama, United States
- Medical Dermatology Specialists Phoenix, Arizona, United States
- Southwest Skin Specialists Phoenix, Arizona, United States
- US Dermatology Partners Sun City West Sun City West, Arizona, United States
NCT05353192
- Conditions
- Achondroplasia, Bone Diseases, Bone Diseases, Developmental, +5 more
- Locations
-
- Children's Hospital of Fudan University Shanghai, Shanghai Municipality, China
Related conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities (12578)
- Nervous System Diseases (4111)
- Nutritional and Metabolic Diseases (3434)
- Metabolic Diseases (3244)
- Skin and Connective Tissue Diseases (2592)
- Hemic and Lymphatic Diseases (2485)
- Metabolism, Inborn Errors (2469)
- Hematologic Diseases (2272)