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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,530 public trials 2,140 recruiting studies
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Genetic Diseases, Inborn trial results

Recruiting

A Study of VERVE-102 in Patients With Familial Hypercholesterolemia or Premature Coronary Artery Disease

NCT06164730

Conditions
Arterial Occlusive Diseases, Arteriosclerosis, Cardiovascular Diseases, +18 more
Locations
  • Clinical Study Center Dothan, Alabama, United States
  • Clinical Study Center Pomona, California, United States
  • Clinical Study Center Boca Raton, Florida, United States
  • Clinical Study Center Jacksonville, Florida, United States
View all 24 locations
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Recruiting

Study of ARO-DIMERPA in Adult Participants With Mixed Hyperlipidemia

NCT07223658

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Genetic Diseases, Inborn, +9 more
Locations
  • Research Site 7 Charlestown, New South Wales, Australia
  • Research Site 5 Morayfield, Queensland, Australia
  • Research Site 8 East Melbourne, Victoria, Australia
  • Research Site 4 Melbourne, Victoria, Australia
View all 15 locations
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Recruiting

A Clinical Trial of PR001 (LY3884961) in Patients With Peripheral Manifestations of Gaucher Disease (PROCEED)

NCT05487599

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Cedars-Sinai Los Angeles, California, United States
  • Ann and Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • Duke University Health System Durham, North Carolina, United States
  • Lysosomal & Rare Disorders Research and Treatment Center Fairfax, Virginia, United States
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Recruiting

A Study to Investigate the Efficacy, Safety and Tolerability of Votoplam in Participants With Huntington's Disease

NCT07326709

Conditions
Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +13 more
Locations
  • University of CA San Diego La Jolla, California, United States
  • CenExcel Rocky Mtn Clin Research Englewood, Colorado, United States
  • Georgetown University Washington D.C., District of Columbia, United States
  • University Of South Florida Tampa, Florida, United States
View all 41 locations
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Recruiting

Clinical Trial in Patients With Barth Syndrome- 4TAZPower

NCT07531251

Conditions
Abnormalities, Multiple, Barth Syndrome, Cardiovascular Abnormalities, +12 more
Locations
  • Trial Not Offered in the U.S Needham, Massachusetts, United States
  • Metabolics and Genetics in Canada (MAGIC) Calgary, Alberta, Canada
  • Bristol Royal Hospital for Children Upper Maudlin Street Paul O'Gorman Building Bristol, United Kingdom
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Recruiting

A Study to Assess the Effects of ACI-24.060 in Alzheimer's Disease and in Down Syndrome (ABATE Study)

NCT05462106

Conditions
Abnormalities, Multiple, Alzheimer Disease, Alzheimer's Disease, +23 more
Locations
  • Barrow Neurological Institute Phoenix, Arizona, United States
  • K2 Medical Research The Villages LLC Lady Lake, Florida, United States
  • Charter Research, LLC Orlando, Florida, United States
  • Headlands Horizons LLC Orlando, Florida, United States
View all 26 locations
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Recruiting

A Study of AMG 732 in Healthy Participants and Participants With Thyroid Eye Disease

NCT06401044

Conditions
Autoimmune Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Endocrine System Diseases, +12 more
Locations
  • Applied Research Center of Arkansas Little Rock, Arkansas, United States
  • Amy Patel Jain MD Newport Beach, California, United States
  • Levenson Eye Associates Jacksonville, Florida, United States
  • Ilumina Medical Research Kissimmee, Florida, United States
View all 44 locations
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