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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,559 public trials 2,153 recruiting studies
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Genetic Diseases, Inborn trial results

Recruiting

HPC Offered for PRESERVE Expansion

NCT07145411

Conditions
Anemia, Anemia, Aplastic, Anemia, Hemolytic, +31 more
Locations
  • University of Alabama, Birmingham Birmingham, Alabama, United States
  • Henry Ford Health Detroit, Michigan, United States
  • The Ohio State University Medical Center Columbus, Ohio, United States
  • Tristar Centennial Medical Center Nashville, Tennessee, United States
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Recruiting

Phase 1 Study of GC1130A in Patients With Sanfilippo Syndrome Type A (MPS IIIA)

NCT06567769

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • UCSF Benioff Children's Hospital Oakland, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • National Center for Child Health and Development Setagaya City, Tokyo, Japan
  • Ajou University Medical Center Suwon, Gyeongi-do, South Korea
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Recruiting

A Safety and Pharmacokinetics Trial of VO659 in SCA1, SCA3 and HD

NCT05822908

Conditions
Ataxia, Basal Ganglia Diseases, Brain Diseases, +23 more
Locations
  • Rigshospitalet Copenhagen, Denmark
  • Centre Hospitalier Universitaire dÁngers Angers, France
  • CHU Gui de Chauliac Montpellier- Expert Center of Neurogenetic diseases, Department of Neurology Montpellier, France
  • Universtiry Hospitals Pitie Salpetriere - Charles foix - Paris Paris, France
View all 14 locations
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