Completed
Gene Replacement Therapy Clinical Trial for Participants With Spinal Muscular Atrophy Type 1
NCT03306277
- Conditions
- Central Nervous System Diseases, Gene Therapy, Motor Neuron Disease, +6 more
- Locations
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- David Geffen School of Medicine at UCLA Los Angeles, California, United States
- Stanford University Stanford, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Nemours Children's Hospital Orlando, Florida, United States