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Clinical trial condition

Gene Therapy

Explore clinical trials studying Gene Therapy. Study availability and eligibility vary by location and protocol.

14 public trials 6 recruiting studies

Gene Therapy trial results

Conditions
Central Nervous System Diseases, Gene Therapy, Motor Neuron Disease, +6 more
Locations
  • David Geffen School of Medicine at UCLA Los Angeles, California, United States
  • Stanford University Stanford, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Nemours Children's Hospital Orlando, Florida, United States
View all 16 locations
Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +8 more
Locations
  • St. Jude Children's Research Hospital Memphis, Tennessee, United States
  • Civil Service Hospital Kathmandu, Nepal
  • Hospital Dos De Mayo Lima, Peru
  • National Hospital of Sri Lanka Colombo, Sri Lanka
Conditions
Adeno-Associated Virus (AAV), Blood Coagulation Disorder, Blood Coagulation Disorders, +18 more
Locations
  • Orthopaedic Institute for Children Los Angeles, California, United States
  • Illinois Bleeding and Clotting Disorders Institute Peoria, Illinois, United States
  • University of Michigan Ann Arbor, Michigan, United States
  • Mississippi Center for Advanced Medicine Madison, Mississippi, United States
Conditions
Age-Related Maculopathies, Age-Related Maculopathy, Eye Diseases, +13 more
Locations
  • investigational site number 03WilmerEy Baltimore, Maryland, United States
  • investigational site number 02Ophthalm Boston, Massachusetts, United States
  • investigational site number 01UMassMem Worcester, Massachusetts, United States
  • investigational site number 05RetinaCo Slingerlands, New York, United States