Active, not recruiting
Study to Evaluate the Efficacy and Safety of Venglustat in Adult and Pediatric Patients With Gaucher Disease Type 3
NCT05222906
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
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- Yale University School of Medicine - Investigational Site Number: 8400003 New Haven, Connecticut, United States
- University of Iowa - Investigational Site Number: 8400002 Iowa City, Iowa, United States
- Texas Oncology - Medical City Dallas Site Number : 8400008 Dallas, Texas, United States
- Lysosomal & Rare Disorders Research & Treatment Center, Inc - Investigational Site Number: 8400001 Fairfax, Virginia, United States