NCT04532047
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +39 more
- Locations
-
- University of California San Francisco, California, United States
Clinical trial condition
Gaucher Disease, Type 2
Explore clinical trials studying Gaucher Disease, Type 2. Study availability and eligibility vary by location and protocol.
3 public trials
1 recruiting study
Gaucher Disease, Type 2 trial results
NCT04470713
- Conditions
- AB Variant Gangliosidosis GM2, Brain Diseases, Brain Diseases, Metabolic, +24 more
- Locations
-
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Mayo Clinic - Rochester Rochester, Minnesota, United States
- Lysosomal and Rare Disorders Research and Treatment Center Fairfax, Virginia, United States
- UCL Cliniques Universitaires Saint-Luc Brussels, Belgium
Active, Not Recruiting
Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE)
NCT04411654
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- UCSF Benioff Children's Hospital, 747 52nd St Oakland, California, United States
- University of Minnesota Masonic Children's Hospital, 2450 Riverside Avenue Minneapolis, Minnesota, United States
- Children's Hospital of Pittsburgh, 4401 Penn Avenue Pittsburgh, Pennsylvania, United States
- Lysosomal & Rare Disorders Research and Treatment Center Fairfax, Virginia, United States