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Clinical trial condition

Gaucher Disease, Type 1

Explore clinical trials studying Gaucher Disease, Type 1. Study availability and eligibility vary by location and protocol.

20 public trials 2 recruiting studies

Gaucher Disease, Type 1 trial results

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Cedars-Sinai Los Angeles, California, United States
  • Ann and Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • Duke University Health System Durham, North Carolina, United States
  • Lysosomal & Rare Disorders Research and Treatment Center Fairfax, Virginia, United States
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Kaiser Permanente Los Angeles, California, United States
  • Lysosomal Rare Disorders Research and Treatment Center Fairfax, Virginia, United States
  • Hospital de Clinicas de Porto Alegre (HCPA) Porto Alegre, Brazil
  • SphinCS Höchheim, Germany
Conditions
3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more
Locations
  • CRMN, Hôpital La Citadelle Liège, Wallonia, Belgium
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Hipolito Yrigoyen Buenos Aires, Argentina
  • Shaare Zedek Medical Center Jerusalem, Israel
  • Sociedad Espanola de Socorros Mutuos Asunción, Paraguay
  • National Research Center for Haematology Moscow, Russia
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Los Angeles Medical Center Los Angeles, California, United States
  • Children's Hospital Oakland Oakland, California, United States
  • Emory University School of Medicine Atlanta, Georgia, United States
  • Children's Memorial Hospital Chicago, Illinois, United States
View all 21 locations