NCT05487599
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
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- Cedars-Sinai Los Angeles, California, United States
- Ann and Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Duke University Health System Durham, North Carolina, United States
- Lysosomal & Rare Disorders Research and Treatment Center Fairfax, Virginia, United States