Active, not recruiting
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)
NCT05230459
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, FKRP, FKRP Mutation, +17 more
- Locations
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- University of California - Irvine Irvine, California, United States
- University of Iowa Iowa City, Iowa, United States
- University of Kansas Medical Center Kansas City, Kansas, United States
- Kennedy Krieger Institute Baltimore, Maryland, United States