NCT03876522
- Conditions
- Brain Diseases, Carbohydrate Metabolism, Inborn Errors, Central Nervous System Diseases, +19 more
- Locations
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- IONIS Investigative Site Los Angeles, California, United States
- IONIS Investigative Site Dallas, Texas, United States
- IONIS Investigative Site Bologna, Italy
- IONIS Investigative Site Madrid, Spain