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Clinical trial condition

Cystinosis

Explore clinical trials studying Cystinosis. Study availability and eligibility vary by location and protocol.

41 public trials 9 recruiting studies
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Cystinosis trial results

Completed

Open-Label, Safety and Superior Effectiveness Study of Cysteamine Bitartrate Delayed-Release Capsules (RP103) in Cystinosis

NCT01733316

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Disease Attributes, +8 more
Locations
  • California Pacific Medical Center (CPMC) Research Institute San Francisco, California, United States
  • Stanford University Medical School Stanford, California, United States
  • Emory Children's Center Atlanta, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
View all 14 locations
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Completed

Phase 3 Study of Cysteamine Bitartrate Delayed-release (RP103) Compared to Cystagon® in Patients With Cystinosis

NCT01000961

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Disease Attributes, +8 more
Locations
  • Stanford University Medical School Stanford, California, United States
  • Emory Children's Center Atlanta, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago (formerly Children's Memorial Hospital) Chicago, Illinois, United States
  • Hospices Civils de Lyon Lyon, France
View Trial Details
Completed

Cystadrops in Pediatric Cystinosis Patients From Six Months to Less Than Two Years Old (SCOB2)

NCT04125927

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Genetic Diseases, Inborn, +4 more
Locations
  • UZ Leuven Leuven, Belgium
  • Hôpital Necker-Enfants Malades Paris, France
  • Klinik für Pädiatrische Nieren Hanover, Germany
  • Bambin Gesù Hospital in Palidoro Roma, Italy
View Trial Details
Completed

Genetic Newborn Screening for Cystinosis and Spinal Muscular Atrophy

NCT06027385

Conditions
Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, +13 more
Locations
  • RoMed Hospital Rosenheim, Bavaria, Germany
  • University Hospital Essen, Center for Pediatrics and Adolescent Medicine Essen, Germany
  • Dr. von Haunersches Kinderspital München, Germany
  • University Hospital Münster, Clinic and Polyclinic for Pediatrics and Adolescent Medicine Münster, Germany
View Trial Details
Completed

A Protocol to Allow Treatment With ICL670 for Patients With or at Risk of Life-threatening Complications of Transfusional Iron Overload Who Are Unable to Tolerate Other Iron Chelators Because of Documented Severe Toxicity

NCT01044186

Conditions
Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +19 more
Locations
  • Children's Hospital and Research Center - Oakland Oakland, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Children's Hospital Boston Boston, Massachusetts, United States
  • Queens Hospital Center Jamaica, New York, United States
View all 18 locations
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