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Congenital Bone Marrow Failure Syndromes

Clinical trial condition

Congenital Bone Marrow Failure Syndromes

Explore clinical trials studying Congenital Bone Marrow Failure Syndromes. Study availability and eligibility vary by location and protocol.

106 public trials 18 recruiting studies

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Congenital Bone Marrow Failure Syndromes trial results

Completed

Baby Detect : Genomic Newborn Screening

NCT05687474

Conditions: 3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more
Locations: CRMN, Hôpital La Citadelle Liège, Wallonia, Belgium

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Completed

Corrective Exercise and Rehabilitation in Fanconi Anemia: A Case Study

NCT06958380

Conditions: Anemia, Anemia, Aplastic, Anemia, Hypoplastic, Congenital, +14 more
Locations: Pardis specialized wellness institute Isfahan, Iran

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Completed

Hematopoietic Stem Cell Transplant for Dyskeratosis Congenita or Severe Aplastic Anemia

NCT02162420

Conditions: Anemia, Anemia, Aplastic, Aplastic Anemia, +14 more
Locations: University of Minnesota Medical Center, Fairview Minneapolis, Minnesota, United States

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Completed

Treatment of Refractory Diamond-Blackfan Anemia With Eltrombopag

NCT04269889

Conditions: Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +9 more
Locations: National Institutes of Health Clinical Center Bethesda, Maryland, United States

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Completed

Needs Assessment for Individuals and Families Affected by Dyskeratosis Congenita (DC) and Related Telomere Biology Disorders (TBD)

NCT04959188

Conditions: Bone Marrow Diseases, Bone Marrow Failure Disorders, Congenital Abnormalities, +12 more
Locations: National Cancer Institute (NCI) Bethesda, Maryland, United States

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Completed

Risk-Adapted Allogeneic Stem Cell Transplantation For Mixed Donor Chimerism In Patients With Non-Malignant Diseases

NCT01019876

Conditions: Anemia, Anemia, Aplastic, Anemia, Hypoplastic, Congenital, +23 more
Locations: Columbia University Medical Center New York, United States

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Completed

Time-restricted Feeding to Reduce Inflammation in Fanconi Anemia

NCT05598515

Conditions: Anemia, Anemia, Aplastic, Anemia, Hypoplastic, Congenital, +11 more
Locations: Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States

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Completed

Prognostic Significance of Mutation Type and Chromosome Fragility in Fanconi Anemia

NCT06490510

Conditions: Anemia, Anemia, Aplastic, Anemia, Hypoplastic, Congenital, +11 more
Locations: Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau - IIB Sant Pau Barcelona, Spain

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Completed

Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A

NCT03157804

Conditions: Anemia, Anemia, Aplastic, Anemia, Hypoplastic, Congenital, +11 more
Locations: Hospital Vall d'Hebron Barcelona, Spain

Hospital Infantil del Niño Jesus Madrid, Spain

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Completed

Quercetin in Children With Fanconi Anemia; a Pilot Study

NCT01720147

Conditions: Anemia, Anemia, Aplastic, Anemia, Hypoplastic, Congenital, +11 more
Locations: Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States

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Congenital Bone Marrow Failure Syndromes

Congenital Bone Marrow Failure Syndromes trial results

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