NCT03597399
- Conditions
- Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, +7 more
- Locations
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- Children's Hospital of Los Angeles Los Angeles, California, United States
- Bascom Palmer Eye Institute Miami, Florida, United States
- University of Iowa Hospitals & Clinics Iowa City, Iowa, United States
- Massachusetts Eye and Ear Institute Boston, Massachusetts, United States