Enrolling by Invitation
Long-term Extension of GTX-102 in Angelman Syndrome
NCT06415344
- Conditions
- Abnormalities, Multiple, Angelman Syndrome, Central Nervous System Diseases, +7 more
- Locations
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- University of California, Los Angeles (UCLA) Los Angeles, California, United States
- University of California, San Diego - Rady Children's Hospital San Diego, California, United States
- Rare Disease Research, LLC Atlanta, Georgia, United States
- Rush University Medical Center Chicago, Illinois, United States