Active, Not Recruiting
CAMPSIITE™ RGX-121 Gene Therapy in Subjects With MPS II (Hunter Syndrome)
NCT03566043
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- University of California San Francisco, Benioff Children's Hospital Oakland, California, United States
- St. Peter's University Hospital New Brunswick, New Jersey, United States
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
- Children's Hospital of Pittsburgh - UPMC: Program for Neurodevelopment in Rare Disorders Pittsburgh, Pennsylvania, United States