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Clinical trial condition

Brain Diseases, Metabolic, Inborn

Explore clinical trials studying Brain Diseases, Metabolic, Inborn. Study availability and eligibility vary by location and protocol.

949 public trials 197 recruiting studies
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Brain Diseases, Metabolic, Inborn trial results

Completed

Evaluation of the Long-term Safety, Pharmacodynamics, and Exploratory Efficacy of GZ/SAR402671 in Treatment-Naïve Adult Male Patients With Fabry Disease

NCT02489344

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Investigational Site Number 840002 Atlanta, Georgia, United States
  • Investigational Site Number 840003 Cincinnati, Ohio, United States
  • Investigational Site Number 840001 Fairfax, Virginia, United States
  • Investigational Site Number 250001 Garches, France
View Trial Details
Completed

Home Therapy With VPRIV in Gaucher's Disease

NCT01356537

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • Landeskrankenhaus Bregenz Bregenz, Austria
  • Paracelsus Medizinische Privatuniversität Salzburg Salzburg, Austria
  • AKH, Allgemeines Krankenhaus der Stadt Wien Vienna, Austria
  • Medical University of Vienna Vienna, Austria
View Trial Details
Completed

Home Therapy With Replagal in Fabry Disease

NCT01355146

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Landeskrankenhaus Bregenz Bregenz, Austria
  • LKH-Universitätsklinikum Graz Graz, Austria
  • Paracelsus Medizinische Privatuniversität Salzburg Salzburg, Austria
  • Universitätsklinik für Innere Medizin III Vienna, Austria
View all 22 locations
View Trial Details
Completed

Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia

NCT01599286

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +21 more
Locations
  • University of California Los Angeles Los Angeles, California, United States
  • Lucile Packard Children's Hospital at Stanford Palo Alto, California, United States
  • The Children's Hospital of Colorado Aurora, Colorado, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
View Trial Details
Completed

Long-term Outcome in Late-onset Pompe Disease Treated Beyond 36 Months (STIG-Pompe-Study)

NCT02824068

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
Locations
  • Friedrich-Baur-Institute, Dep. of Neurology Klinikum der Universitaet Muenchen Munich, Germany Munich, Bavaria, Germany
  • 5. Department of Clinical and Experimental Medicine, Reference Center for Rare Neuromuscular Disorders, University of Messina, Italy Messina, Sicily, Italy
  • National Taiwan University Hospital Taipei Taipei, Taiwan
View Trial Details

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