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Clinical trial condition

Brain Diseases, Metabolic, Inborn

Explore clinical trials studying Brain Diseases, Metabolic, Inborn. Study availability and eligibility vary by location and protocol.

949 public trials 197 recruiting studies
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Brain Diseases, Metabolic, Inborn trial results

Completed

Replagal Enzyme Replacement Therapy for Children With Fabry Disease

NCT00084084

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • Tucson Access Center of Arizona Kidney Disease Hypertension Center Tucson, Arizona, United States
  • University of Arizona Health Sciences Center Tucson, Arizona, United States
  • Children's Physician Group Palm Beach Gardens, Florida, United States
  • Christus St. Patrick Hospital Lake Charles, Louisiana, United States
View all 14 locations
View Trial Details
Completed

PKU Skin Stripping

NCT04368624

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +9 more
Locations
  • Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
View Trial Details
Completed

This Study is Designed to Evaluate PD/PK and Safety of Replagal Manufactured by Two Different Processes.

NCT01304277

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of Alberta Hospital Edmonton, Alberta, Canada
  • Queen Elizabeth II Health Sciences Centre Halifax, Nova Scotia, Canada
  • The Hospital for Sick Children Toronto, Ontario, Canada
  • INC Research Toronto, Ontario, Canada
View Trial Details
Completed

Alglucosidase Alfa Pompe Safety Sub-Registry

NCT01710813

Conditions
Anaphylaxis, Brain Diseases, Brain Diseases, Metabolic, +17 more
Locations
  • Investigational Site Number 840016 Phoenix, Arizona, United States
  • Investigational Site Number 840002 Durham, North Carolina, United States
  • Investigational Site Number 840004 Hershey, Pennsylvania, United States
  • Investigational Site Number 840014 Pittsburgh, Pennsylvania, United States
View all 18 locations
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Completed

A Study of Gene-Activated® Human Glucocerebrosidase (GA-GCB) Enzyme Replacement Therapy in Gaucher Disease

NCT00430625

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Hipolito Yrigoyen Buenos Aires, Argentina
  • Shaare Zedek Medical Center Jerusalem, Israel
  • Sociedad Espanola de Socorros Mutuos Asunción, Paraguay
  • National Research Center for Haematology Moscow, Russia
View Trial Details

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