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Clinical trial condition

Brain Diseases, Metabolic, Inborn

Explore clinical trials studying Brain Diseases, Metabolic, Inborn. Study availability and eligibility vary by location and protocol.

949 public trials 197 recruiting studies
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Brain Diseases, Metabolic, Inborn trial results

Completed

Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function

NCT02795676

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +29 more
Locations
  • UAB Medicine Birmingham, Alabama, United States
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • University of California Irvine Center Orange, California, United States
  • University of California San Diego San Diego, California, United States
View all 29 locations
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Completed

Extension Study of PRX-102 for up to 60 Months

NCT01981720

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of Florida Gainesville, Florida, United States
  • University of Iowa Hospitals and Clinics Iowa City, Iowa, United States
  • Johns Hopkins University School of Medicine Baltimore, Maryland, United States
  • Institute of Metabolic Disease Dallas, Texas, United States
View Trial Details
Completed

Simplified Diet Approach in Phenylketonuria

NCT02555579

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
Locations
  • Monroe-Meyer Insititute Omaha, Nebraska, United States
  • Children's Hospital & Medical Center Omaha, Nebraska, United States
  • Nebraska Medicine, Midtown Health Center Omaha, Nebraska, United States
  • Unversity of Nebraska Medical Center Omaha, Nebraska, United States
View Trial Details
Completed

A Prospective and Retrospective Cohort Study in Patients With Chronic Forms of Acid Sphingomyelinase Deficiency (ASMD)

NCT04106544

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • Investigational Site Number :8400002 Atlanta, Georgia, United States
  • Investigational Site Number :8400003 The Bronx, New York, United States
  • Investigational Site Number :8400001 Valhalla, New York, United States
  • Investigational Site Number :0320002 CABA, Argentina
View all 28 locations
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Completed

A Study of AEB1102 (Pegzilarginase) in Patients With Arginase I Deficiency

NCT03378531

Conditions
Amino Acid Metabolism, Inborn Errors, Arginase I Deficiency, Brain Diseases, +11 more
Locations
  • Stanford University School of Medicine Stanford, California, United States
  • University of Florida Gainesville, Florida, United States
  • Icahn School of Medicine at Mount Sinai New York, United States
  • UTSW Dallas, Texas, United States
View Trial Details

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