Skip to main content
OpenTrials

Clinical trial condition

Brain Diseases, Metabolic, Inborn

Explore clinical trials studying Brain Diseases, Metabolic, Inborn. Study availability and eligibility vary by location and protocol.

949 public trials 197 recruiting studies
Refine in advanced search Browse all conditions

Brain Diseases, Metabolic, Inborn trial results

Completed

A Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD)

NCT03852498

Conditions
Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
Locations
  • Lucile Packard Children's Hospital Palo Alto, California, United States
  • Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Hôpital Robert Debré Paris, France
View Trial Details
Completed

Pompe Lactation Sub-Registry

NCT00566878

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
Locations
  • Registry participation is worldwide. Facilities not yet active may enroll upon identification of a patient Cambridge, Massachusetts, United States
  • Grand Rapids, Michigan, United States
View Trial Details
Completed

N-Acetyl-L-Leucine for GM2 Gangliosidosis (Tay-Sachs and Sandhoff Disease)

NCT03759665

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more
Locations
  • University of California - Los Angeles Los Angeles, California, United States
  • Mayo Clinic Rochester, Minnesota, United States
  • NYU Langone School of Medicine New York, United States
  • University of Giessen Giessen, Germany
View Trial Details

Related conditions